The registry is essential for the development of new treatments that combat neuromuscular diseases
Neuromuscular diseases are rare, but often serious. Some of them are fatal. They can affect children or adults, and are characterised by a loss of strength that generates disability and suffering on a daily basis. Few treatments are available, but scientific research is very active and making headway every year. Researchers are constantly looking for patients to take part in therapeutic trials. Joining the registry allows us to tell your doctor if a new treatment could be tried to treat your disease.